A Personalized RNA Therapeutic Treats Twins with Ultra-Rare Form of Batten Disease

A therapeutic developed by Michigan Medicine’s Michelle Hastings, Ph.D., over the last twenty years is not only being used to treat a rare form of juvenile Batten disease but could also be used to target both rare and common diseases for which there is a known genetic cause. Read more about how Hastings developed the therapy, how she is helping two twins with Batten disease, and potential future therapeutic applications.